In a world first, a bespoke gene-editing therapy benefitted one child. Now reseachers plan to launch a clinical trial of the ...

The vestibular system is responsible for the sense of balance in the inner ear. Prolonged use of toxic substances, such as certain antibiotics or anticancer drugs, can damage the hair cells that form ...

The vestibular system is responsible for the sense of balance in the inner ear. Prolonged use of toxic substances, such as ...

In 1962, a pediatric neurology resident at Columbia's Neurological Institute and his colleagues in the College of Physicians ...

EU approves Alexion’s Koselugo for plexiform neurofibromas in adults with neurofibromatosis type 1: Cambridge, UK Wednesday, October 29, 2025, 11:00 Hrs [IST] Alexion, AstraZene ...

Alexion, AstraZeneca Rare Disease's Koselugo (selumetinib), an oral, selective MEK inhibitor, has been approved in the ...

UK pharma major AstraZeneca’s rare disease unit Alexion today revealed that Koselugo (selumetinib), its oral, selective MEK ...

Investing.com -- AstraZeneca PLC (ST:AZN) announced Tuesday that its drug Koselugo (selumetinib) has received European Union ...

AstraZeneca (($AZN)) announced an update on their ongoing clinical study. In a recent update, AstraZeneca announced a new clinical study titled ...

Former New York Jets center Nick Mangold died Saturday night from complications of kidney disease, the team announced Sunday.

A man with neurofibromas who didn't know he's been clinically diagnosed with NF1, learns he harbors a deeply intronic, likely ...

Despite the recent attention to the potential of developing and using gene therapy to treat several diseases, the therapy was ...