Scholar Rock intends to resubmit the apitegromab Biologics License Application (BLA) upon resolution of Catalent Indiana LLC-related observations Scholar Rock (NASDAQ: SRRK), a global ...

A new clinical trial has revealed encouraging results for a muscle-targeting therapy aimed at improving motor function in children and adolescents with spinal muscular atrophy, according to a study ...

There is no cure for DMD, but treatments can slow the progression of the disease and help improve quality of life. Duchenne muscular dystrophy (DMD) is a chronic condition that causes a gradual loss ...

“His whole childhood was spent waiting for things to get better,” Gillian Morrison said after her son Harvey’s death Courtesy of Gillian Morrison Harvey Morrison was born with severe scoliosis and ...

Harvey Morrison was born with severe scoliosis and needed a spinal surgery that was “a matter of life and death” His surgery was constantly rescheduled and, at one point, he was even unknowingly ...

Oral risdiplam (Evrysdi, Genentech) started in the first 6 weeks of life let most infants with presymptomatic spinal muscular atrophy (SMA) reach motor milestones typical of healthy babies, results of ...

COLORADO (KRDO) – Thirteen-year-old Nora Casper knows firsthand how scary spine surgery can be. Diagnosed with congenital scoliosis as a baby, she’s undergone multiple spinal procedures, including her ...

MONROE COUNTY, Tennessee — The school year is underway at Sequoyah High School in Madisonville. For Sophomores Bristol Williams and Jett Trammell, the first week of the new year was also an ...

DENVER (KDVR) — A breakthrough new procedure pioneered by a group of doctors in Colorado is offering new hope for some teenagers living with scoliosis. Vertebral body tethering is a surgical treatment ...

Vertebral body tethering is a surgical treatment option for scoliosis in growing children whose scoliosis — or spine curvature — continues to progress despite wearing a brace. FOX31's Christine Noel ...