Dec 22, 2025 · Our pipeline includes investigational medicines across four areas of focus: central nervous system, cardiovascular, musculoskeletal/metabolic and non-oncology hematology.

We leverage expertise in genetics and genomics to create new medicines for people with serious medical conditions. Learn more about our products and pipeline.

The BioMarin Medical website is intended for use by healthcare professionals and provides a broad range of resources, including publications, congress and pipeline information, posters …

Home Products & Pipeline Products We provide eight important treatment options for people living with serious medical conditions. Learn more about our marketed products below. Note: The …

Mar 31, 2025 · The San Rafael, California -based company, founded in 1997, has a proven track record of innovation with eight commercial therapies and a strong clinical and preclinical pipeline.

Feb 19, 2025 · The San Rafael, California -based company, founded in 1997, has a proven track record of innovation with eight commercial therapies and a strong clinical and preclinical pipeline.

Feb 19, 2025 · The San Rafael, California-based company, founded in 1997, has a proven track record of innovation with eight commercial therapies and a strong clinical and preclinical pipeline.

Dec 19, 2025 · With extraordinary patient focus, Amicus Therapeutics is committed to advancing and expanding a pipeline of cutting-edge, first- or best-in-class medicines for rare diseases.

Jun 30, 2025 · "We were very pleased with our second quarter performance across all aspects of the business, including strong growth, exciting pipeline progress, and delivery of our business …

Pipeline and Clinical Development Programs At BioMarin, we push the boundaries of medical possibility to make a transformative impact. We are dedicated to improving the lives of …